Welcome to our Gene Therapy Center! 


Breakthrough Research

Developing therapeutics for rare genetic disorders

The Faculty of the Horae Gene Therapy Center is dedicated to develop therapeutic approaches for rare inherited diseases for which there is no cure utilizing state of the art technologies to correct the genetic mutations. Our focus is on Canavan DiseaseTay-Sachs & Sandhoff diseasesRetinitis PigmentosaCystic FibrosisLou Gehrig's diseaseHuntington's disease, as well as therapies for the more common diseases such as Hypercholesterimia and Cardiac arrhythmia

Learn More


Supportive Ecosystem

We are part of the Advanced Therapeutics Cluster (ATC)

Under the umbrella of the ATC, UMass Medical School formed the Gene Therapy Center (GTC) emphasizing the promise that lies within the application of the recombinant adeno-associated virus; RNA Therapeutics Institute (RTI) featuring novel strategies for using the RNAi mechanism to silence the action of individual genes and The Center for Stem Cell Biology and Regenerative Medicine seeking to unlock the enormous promise to elucidate disease mechanisms inherent in humans.

 Learn More


Partner Opportunities

Learn more how we can partner together

The Horae Gene Therapy Center is always interested in possible partnerships with both indivituals and organizations. Some possible partnerships include knowledge exchangeconsultingcollaborations with academia and/or industryreagent exchangesponsored research, and spinout activities. We encourage you to contact us and learn more how we can partner together to advance the area of gene therapy.

 Learn More



We believe that great scientific discoveries happen when people collaborate.

Let's have the next big breakthrough together!


Partner with Us





▴ Back To Top
Section Menu To Top