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Spotlight on Gene Therapy: finding a Cure

Gene Therapy Treatment for SOD1 ALS

Posted On: Thursday, December 31, 2015 Posted By: Florie Borel Tags: Adeno-associated virus, Amyotrophic lateral sclerosis, Gene Therapy, Publications

Our lab published "Therapeutic rAAVrh.10-mediated SOD1 silencing in adult SOD1G93A mice and non-human primates". We are also making the cover of the January issue of Human Gene Therapy! Full text available here.

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New publication on ALS

Posted On: Tuesday, December 01, 2015 Posted By: Florie Borel Tags: Amyotrophic lateral sclerosis, Publications

Our lab in collaboration with the lab of Dr. Brown published "Human C9ORF72 Hexanucleotide Expansion Reproduces RNA Foci and Dipeptide Repeat Proteins but Not Neurodegeneration in BAC Transgenic Mice".

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