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Spotlight on Gene Therapy: finding a Cure

Today is Rare Disease Day

Posted On: Tuesday, February 28, 2017 Posted By: Florie Borel Tags: Alpha-one antitrypsin, Amyotrophic lateral sclerosis, Cystic fibrosis

Today is Rare Disease Day! Share the link below and raise awareness about rare diseases!

RareDiseaseDay.org

Did you know that rare diseases are estimated to affect about 1 in 15 persons worldwide? That's more than 400 millions people!

Rare Disease Day 2017

Our lab is dedicated to rare disease research, we develop gene therapy treatments for amyotrophic lateral sclerosis (ALS), alpha-1 antitrypsin deficiency, and Huntington's disease. We are also involved in research on cystic fibrosis, and Hermansky-Pudlak syndrome.

For more news on rare disease research and on gene therapy, you can also follow our Facebook page @muellerlab and our Twitter account @muellerlab !