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Spotlight on Gene Therapy: finding a Cure

Mueller Lab at ASGCT

Posted On: Tuesday, April 26, 2016 Posted By: Florie Borel Tags: Adeno-associated virus, Alpha-one antitrypsin, Amyotrophic lateral sclerosis, Gene Therapy, Immunology, Presentations

The Mueller Lab will be presenting its research at ASGCT 2016, May 4-7 in Washington, DC.

Wednesday, May 4

AAV Vectors I: Gwladys Gernoux will be presenting "Vector Biodistribution After Recombinant AAVrh10 Intrathecal Delivery in Non-Human Primates"

Diabetes, Metabolic and Genetic Diseases I: Florie Borel will be presenting "Genome Editing to Generate the First Mouse Model of Alpha-One Antitrypsin Deficiency, the Leading Cause of Genetic COPD"

Thursday, May 5

Scientific Symposium 202, Chris Mueller will be presenting: "Genome Editing the First Animal Model of Emphysema Due to Alpha-1 Antitrypsin Deficiency"

Friday, May 6

Immunological Aspects of Gene Therapy II: AAV Vectors, Gwladys Gernoux will be presenting: "Detection and Isolation of Immune Cells After Intramuscular AAV Injection in Mouse and Human"

Saturday, May 7

Oligonucleotide Therapeutics II, Gabriela Toro will be presenting: "Engineered MicroRNA Silences C9ORF72 Variants in BAC Transgenic Mouse"