RNA Therapeutics Institute
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Neil Aronin, MD
Academic Role: Professor
Programs: Department of Medicine, RNA Therapeutics Institute
Higgins Family Professor of Neuroscience
Focus: Neurodegenerative diseases, especially Parkinson's and Huntington's diseases.
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Robert H. Brown, Jr., MD, DPhil
Academic Role: Professor and Vice Chair
Programs: Department of Biochemistry and Molecular Biotechnology, Department of Neurology, RNA Therapeutics Institute
Leo P. and Theresa M. LaChance Chair in Medical Research
Focus: Identification of gene defects in neuromuscular diseases; Amyotrophic Lateral Sclerosis.
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Fen-Biao Gao, PhD
Academic Role: Professor
Programs: Department of Neurology, RNA Therapeutics Institute
The Governor Paul Cellucci Chair in Neuroscience Research
Focus: Understanding Frontotemporal Dementia (FTD) and ALS.
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Guangping Gao, PhD
Academic Role: Professor
Programs: Department of Microbiology and Physiological Systems, Horae Gene Therapy Center, RNA Therapeutics Institute
Penelope Booth Rockwell Chair in Biomedical Research
Director, Horae Gene Therapy Center
Focus: Adeno-associated virus vectors for gene therapy of genetic diseases including Canavan Disease
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Allan S. Jacobson, PhD
Academic Role: Professor
Programs: Department of Microbiology and Physiological Systems, RNA Therapeutics Institute
Gerald L. Haidak, MD, and Zelda S. Haidak Professorship in Cell Biology (est. 1999)
Focus: Post-transcriptional control of gene expression in model systems and genetic disorders
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Anastasia Khvorova, PhD
Academic Role: Professor
Programs: Program in Molecular Medicine, RNA Therapeutics Institute
Remondi Family Chair in Biomedical Research
Focus: Therapeutic gene silencing in vivo.
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Gary R. Ostroff, PhD
Academic Role: Professor
Programs: Program in Molecular Medicine, RNA Therapeutics Institute
Focus: Using small to macromolecular drug delivery to phagocytes to modulate inflammation and pathologies associated with infectious, autoimmune and neurodegenerative diseases.
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Joel Richter, PhD
Academic Role: Professor
Programs: Program in Molecular Medicine, RNA Therapeutics Institute
Arthur F. Koskinas Chair in Neuroscience
Focus: Translational control in meiosis, mitosis, and neuronal synaptic plasticity. Fragile X syndrome.
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Dan Wang, PhD
Academic Role: Assistant Professor
Programs: RNA Therapeutics Institute
Focus: AAV Gene Therapy for Genetic Diseases
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Jonathan K. Watts, PhD
Academic Role: Associate Professor
Programs: RNA Therapeutics Institute
Focus: Therapeutic gene silencing with chemically modified antisense oligonucleotides.
