Congratulations to Lindsey Wallace and the Scott Harper lab at Nationwide Children’s Hospital for the publication of their paper: “Pre-clinical Safety and Off-Target Studies to Support Translation of AAC-Mediated RNAi Therapy for FSHD” to advance FSHD research towards therapy.
Wallace LM, Saad NY, Pyne NK, Fowler AM, Eidahl JO, Domire JS, Griffin DA, Herman AC, Sahenk Z, Rodino-Klapac LR, Harper SQ. Mol Ther Methods Clin Dev. 2017 Dec 24;8:121-130. doi: 10.1016/j.omtm.2017.12.005. eCollection 2018 Mar 16. PMID: 29387734.