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The Li Weibo (李伟波) Institute for Rare Diseases Research
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Rare Diseases Research
Home
Research News
Faculty
Rare Diseases
Alpha-1 Antitrypsin Deficiency
Amyotrophic Lateral Sclerosis (ALS)
Canavan Disease
CDKL5 Disorder
Chronic Granulomatous
Cockayne Syndrome
Cystic Fibrosis
Down Syndrome
Facioscapulohumeral Muscular Dystrophy
Fanconi Anemia
Fragile X Syndrome
Friedreich’s Ataxia
Frontotemporal Dementia
Gaucher Disease
GM3 Synthase Deficiency
Hereditary Tyrosinemia Type 1
Leber Congenital Amaurosis
Huntington’s Disease
Metabolic Diseases
Retinitis Pigmentosa
Rett Syndrome
Severe Chronic Neutropenia
Sandhoff Disease
Tay-Sachs
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Rare Diseases Research
Home
Research News
Faculty
Rare Diseases
Alpha-1 Antitrypsin Deficiency
Amyotrophic Lateral Sclerosis (ALS)
Canavan Disease
CDKL5 Disorder
Chronic Granulomatous
Cockayne Syndrome
Cystic Fibrosis
Down Syndrome
Facioscapulohumeral Muscular Dystrophy
Fanconi Anemia
Fragile X Syndrome
Friedreich’s Ataxia
Frontotemporal Dementia
Gaucher Disease
GM3 Synthase Deficiency
Hereditary Tyrosinemia Type 1
Leber Congenital Amaurosis
Huntington’s Disease
Metabolic Diseases
Retinitis Pigmentosa
Rett Syndrome
Severe Chronic Neutropenia
Sandhoff Disease
Tay-Sachs
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Alpha-1 Antitrypsin Deficiency
Amyotrophic Lateral Sclerosis (ALS)
Canavan Disease
CDKL5 Disorder
Chronic Granulomatous
Cockayne Syndrome
Cystic Fibrosis
Down Syndrome
Facioscapulohumeral Muscular Dystrophy
Fanconi Anemia
Fragile X Syndrome
Friedreich’s Ataxia
Frontotemporal Dementia
Gaucher Disease
GM3 Synthase Deficiency
Hereditary Tyrosinemia Type 1
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