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Top story: Boston toddler Noa Greenwood, who was one of the first to receive an investigational gene therapy for Canavan disease developed at UMass Chan Medical School, delivered a very special “thank you” to the research team in a visit with her parents earlier this year.

Boston toddler Noa Greenwood, who was one of the first to receive an investigational gene therapy for Canavan disease developed at UMass Chan Medical School, delivered a very special “thank you” to the research team in a visit with her parents earlier this year.

Guangping Gao, PhD, will be honored by the National Tay-Sachs & Allied Diseases Association for his work in identifying the Canavan gene, revitalizing gene therapy, and his many accomplishments leading to potential treatments for Canavan disease.

Gao lab shows AAV gene therapy on path to clinical trial for Canavan disease

Telegram: Rare disease research at UMMS holds deep meaning for families Telegram: Rare disease research at UMMS holds deep meaning for families UMass Medical School Communications UMass Medical School researcher Guangping Gao, PhD, spoke with the Telegram & Gazette about research underway at the Li Weibo Institute for Rare Diseases Research. Guangping Gao, PhD, spoke with the Telegram & Gazette about promising research underway by 40 faculty of the Li Weibo Institute for Rare Diseases Research at

UMass Medical School - Scientist wins award for tackling devastating brain disease in kids | Archives | 2011 Scientist wins award for tackling devastating brain disease in kids Miguel Sena-Esteves     Miguel Sena-Esteves, PhD, associate professor of neurology, was presented with the annual “See the Light” award from the Mathew Forbes Romer Foundation (MFRF) in recognition of his leadership in the fight against children’s genetic diseases of the brain. A member of the UMass Medical School Gene Therapy

Two UMMS gene therapy clinical trials aided by $2 million from FDA’s rare disease grant program2010 03 01James FessendenUMass Medical School CommunicationsTwo clinical trials currently underway at UMass Medical School that are focused on using an adeno associated virus (AAV) to

Three UMMS students traveled to Bolivia for an infectious disease rotation, treating cases considered exotic in the U.S.

Two UMass Medical School researchers report on promising new developments in the quest for a treatment for Huntington’s disease in the Thursday, Nov. 1, issue of the New England Journal of Medicine. Neil Aronin, MD, and Melissa J. Moore, PhD, co-authored an editorial on the latest research into Huntington’s disease, an inherited neurological disorder caused by a mutation on a single chromosome.

Envisioning a cure in rare lung disease - UMass Medical School - Worcester Envisioning a cure in rare lung disease Researchers, families to focus on potential new treatments in Alpha-1 Antitrypsin Deficiency Malorye Branca UMass Medical School Communications Past milestones and future treatment prospects will be described by world-renowned Alpha-1 researchers at a free program at UMMS on Saturday, April 20. Past milestones and future treatment prospects will be described by world-renowned Alpha-1