Horae Gene Therapy Center Faculty

  • Mai ElMallah

    Mai ElMallah, M.D.

    Academic Role: Assistant Professor, Department of Pediatrics, Division of Pulmonary Medicine

    Focus: Gene therapy and neuromodulation for respiratory insufficiency in genetic diseases.  Respiratory physiology and neurophysiology core.

    Email Dr. ElMallah         Faculty Profile

  • Terence  Flotte

    Terence Flotte, M.D.

    Academic Role: Dean School of Medicine, Provost and Executive Deputy Chancellor, Professor, Pediatrics

    Focus: Recombinant adeno-associated virus (AAV) gene therapy vectors for, cystic fibrosis (CF), alpha-1-antitrypsin deficiency (AAT) and fatty oxidation disorders (FAO).

    Email Dr. Flotte            Faculty Profile

  • Guangping Gao

    Guangping Gao, Ph.D.

    Academic Role: Professor Department of Microbiology and Physiological Systems, Director Gene Therapy Center & Vector Core, Scientific Director UMMS-China Translational Research Initiatives

    Focus: Adeno-associated virus vector mediated gene transfer for gene therapy & gene therapy of inherited neurodegenerative Canavan Disease.

    Email Dr. Gao               Faculty Profile

  • Hemant Khanna

    Hemant Khanna, Ph.D.

    Academic Role: Assistant Professor, Department of Ophthalmology

    Focus: Molecular mechanisms and treatment strategies for inherited retinal and macular degenerative diseases.

    Email Dr. Khanna          Faculty Profile          Lab Web-page 

  • Chris Mueller

    Chris Mueller, Ph.D

    Academic Role: Assistant Professor, Department of Pediatrics

    Focus: Developemnt of gene therapeuitc approaches for genetic disorders of the lung, liver and central nervous system.

    Email Dr. Mueller           FacultyProfile          Lab Web-page

  • Claudio Punzo

    Claudio Punzo, Ph.D

    Academic Role: Assistant Professor, Department of Ophthalmology

    Focus: Retinal degenerative diseases that affect photoreceptors such as Retinitis Pigmentosa and Age-Related Macular degeneration.

    Email Dr. Punzo             Faculty Profile          Lab Web-page

  • Miguel Sena-Esteves

    Miguel Sena-Esteves, Ph.D.

    Academic Role: Associate Professor, Department of Neurology

    Focus: Gene therapy approaches for the treatment of neurodegenerative lysosomal storage diseases such as GM1-gangliosidosis and GM2-gangliosidoses (Tay-Sachs and Sandhoff diseases).

    Email Dr. Esteves           Faculty Profile

  • Qiushi Tang

    Qiushi Tang, M.S.

    Academic Role: Instructor, Department of Pediatrics

    Focus: Adeno-associated virus (AAV) gene therapy research for alpha-1-antitrypsin deficiency (AAT) disease.

    Email Ms. Tang              Faculty Profile

  • Jun Xie

    Jun Xie, Ph.D

    Academic Role: Instructor, Department of Microbiology and Physiological Systems

    Focus: AAV vector technology and AAV-mediated miRNA therapeutics.

    Email Dr. Xie                  Faculty Profile

  • Li Zhong

    Li Zhong, M.D

    Academic Role: Research Associate Professor, Department of Pediatrics; Director: Vector development of Vector Core

    Focus: Molecular biology of human parvoviruses and their use as vectors in human gene therapy as well as gene therapy for hematopoietic diseases and neurodegenerative diseases.

    Email Dr. Zhong             Faculty Profile

 Learn more about our affiliated faculty or breakthrough research

   

Affiliated Faculty Our Research 

▴ Back To Top
Section Menu To Top