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The Horae (红瑞) Gene Therapy Center
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Additional Resources
About
Horae GTC Center
Faculty
Faculty Publications
Terence Flotte, MD
Guangping Gao, PhD
Hemant Khanna, PhD
Christian Mueller, PhD
Claudio Punzo, PhD
Miguel Sena-Esteves, PhD
Neil Aronin, MD
Robert Brown, D.Phil, MD
Affiliated Faculty
Affiliates
Bioinformatics
Center for Clinical Translational Science
China Program Office
RNA Therapeutics Institute (RTI)
Sherman Center
Administrative Staff
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Sena-Esteves Lab
Flotte Lab
Gao Lab
Khanna Lab
Mueller Lab
Punzo Lab
Gene Therapy
Research
Alpha-One Antitrypsin Deficiency
Amyotrophic Lateral Sclerosis (ALS)
Canavan Disease
Ciliopathies
Cystic Fibrosis
Fatty Acid Oxidation Deficiencies, VLCAD
Huntington Disease
Hypercholesterimia
Pompe Disease
Retinitis Pigmentosa
Tay-Sachs Disease
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What is a Clinical Trial
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